Business First Real-World Study: Gene Therapy Rollout Timelines for Sickle Cell and Beta Thalassemia by Business Editor — Victoria Nguyen December 7, 2025 by Business Editor — Victoria Nguyen December 7, 2025 Gene Therapy Rollout Highlights Operational Bottlenecks for Rare Disease Treatments Genetix Biotherapeutics Inc., the rebranded successor to bluebird bio, … 0 FacebookTwitterPinterestEmail